[IMAYousaf]

I don't have anything to add except that for some reason, I viscerally remember the first time I heard of Tay-Sachs disease in a high school classroom through a video about genetics.

Something made me feel so disturbed about this one disease above all else because of the seeming hopelessness of the situation coupled with the rampant cruelty of how it kills kids from the inside and seemingly reverses developmental progress.

I don't know why I just remember the moment I learned about this, but this is great news. Hopefully this is the first in many such therapies.